Gene Therapy - Publications - Faculty & Research

27 Sep 2015
News

Pharma gives drug development the Hollywood treatment

07 Feb 2024
News

The Sound of Success

A groundbreaking gene therapy developed by Akouos, Inc., a precision genetic medicine company founded in 2016 by Emmanuel (Manny) Simons (MBA 2012), has enabled an 11-year-old boy from Morocco to hear sounds for the first time. According to a recent New York Times... View Details

01 Oct 2021
News

From Scholarship to Life-Saving Impact

prices and expand access to life-saving therapies,” she says. After college, Rabah joined the biotech company Sio Gene Therapies, where she had the opportunity to speak with parents of children with Tay-Sachs disease, an ultra-rare... View Details

01 Jun 2023
News

From Big Pharma to Startup

Hunter Goble (MBA 2022) did not enroll in Harvard Business School with dreams of becoming an entrepreneur. After earning his MBA, Goble intended to return to Eli Lilly to continue to work building brands and launching products. He envisioned himself leading a big,... View Details

Keywords: April White

01 Dec 2013
News

Innovation as Antidote

inspiration typically comes from a very human place. DART Therapeutics CEO Gene Williams (MBA 1987) ("Your Own Medicine"), for instance, told us about a revelation he had during a 2002 trip to Rotterdam to observe clinical trials for the... View Details

Keywords: Health, Social Assistance

06 Dec 2021
News

Vision: Sound Science

as sound. Getting a healthy copy of the critical gene to the appropriate cells is a solution, but precision inner-ear drug delivery has been a historical stumbling block. An early breakthrough for us was figuring out a way to pair View Details

Keywords: Deb Blagg

01 Dec 2013
News

Your Own Medicine

compounds owned by struggling biotechs. Williams usually calls Tracy once or twice a day, with about a dozen emails back and forth daily. Things are moving. Long term, the Secklers see stem cell or gene replacement View Details

Keywords: Morrell, Daniel; biomedicine; biopharmaceutical company; Ambulatory Health Care Services; Health, Social Assistance

03 Mar 2017
News

Big Blue’s Big Bet

myeloid leukemia, a blood cancer in which abnormal white blood cells grow quickly. They comforted her by saying that the chemotherapy they were prescribing would attack the abnormal cells. And it did. But her recovery from post-remission View Details

Keywords: Paul Kix; illustrations by Dan Page

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